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Titre
Efficacy and safety of migalastat, an oral pharmacologic chaperone for Fabry disease: results from two randomized phase 3 studies, FACETS and ATTRACT
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BSO - Titre
Efficacy and safety of migalastat, an oral pharmacologic chaperone for Fabry disease: results from two randomized phase 3 studies, FACETS and ATTRACT
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DOI
DOI
10.1016/j.ymgme.2016.11.093
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DOAI
DOAI
10.1016/j.ymgme.2016.11.093
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Identifiant WoS
WOS:000393734000086
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Accès ouvert
OA - Non
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Source - Accès ouvert
OA - Non
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Type d'accès
Non OA
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Editeur
Elsevier
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Source
MOLECULAR GENETICS AND METABOLISM
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ISSN
1096-7192
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Type de document
Meeting Abstract
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Notoriété
3 - Correcte
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CNRS
Oui
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CNRS - Institut
INC - Institut de chimie
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uid:/XCQMS3K5
12/10/2021 14:52:35 (latest)
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